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Natalia Niemir Selected Research

Natalia Niemir Research Topics

Disease

3Sandhoff Disease (Sandhoff's Disease)
01/2018 - 01/2013
1Sphingolipidoses (Sphingolipidosis)
08/2014
1GM2 Gangliosidoses (GM2 Gangliosidosis)
08/2014
1Inborn Genetic Diseases (Disease, Hereditary)
08/2014
1Lysosomal Storage Diseases (Lysosomal Storage Disease)
01/2013

Drug/Important Bio-Agent (IBA)

3Hexosaminidases (Hexosaminidase)IBA
01/2018 - 01/2013
2Proteins (Proteins, Gene)FDA Link
08/2014 - 01/2013
2G(M2) Ganglioside (Ganglioside GM2)IBA
08/2014 - 01/2013
1Pyrimethamine (Daraprim)FDA Link
08/2014
1SphingolipidsIBA
08/2014
1EnzymesIBA
01/2013

Therapy/Procedure

1Intravenous Administration
01/2018
1Therapeutics
08/2014